<code id='1CAE9D35C4'></code><style id='1CAE9D35C4'></style>
    • <acronym id='1CAE9D35C4'></acronym>
      <center id='1CAE9D35C4'><center id='1CAE9D35C4'><tfoot id='1CAE9D35C4'></tfoot></center><abbr id='1CAE9D35C4'><dir id='1CAE9D35C4'><tfoot id='1CAE9D35C4'></tfoot><noframes id='1CAE9D35C4'>

    • <optgroup id='1CAE9D35C4'><strike id='1CAE9D35C4'><sup id='1CAE9D35C4'></sup></strike><code id='1CAE9D35C4'></code></optgroup>
        1. <b id='1CAE9D35C4'><label id='1CAE9D35C4'><select id='1CAE9D35C4'><dt id='1CAE9D35C4'><span id='1CAE9D35C4'></span></dt></select></label></b><u id='1CAE9D35C4'></u>
          <i id='1CAE9D35C4'><strike id='1CAE9D35C4'><tt id='1CAE9D35C4'><pre id='1CAE9D35C4'></pre></tt></strike></i>

          focus

          focus

          author:hotspot    Page View:372
          Christine Kao/STAT

          The Food and Drug Administration on Friday approved the world’s first medicine based on CRISPR gene-editing technology, a groundbreaking treatment for sickle cell disease that delivers a potential cure for people born with the chronic and life-shortening blood disorder.

          The new medicine, called Casgevy, is made by Vertex Pharmaceuticals and CRISPR Therapeutics. Its authorization is a scientific triumph for the technology that can efficiently and precisely repair DNA mutations — ushering in a new era of genetic medicines for inherited diseases.

          advertisement

          In a clinical trial, Casgevy was shown to eliminate recurrent episodes of debilitating pain caused by sickle cell, which afflicts approximately 100,000 people in the U.S., a vast majority of whom are Black. The therapy, whose scientific name is exa-cel, is described as a potential cure because the genetic fix enabled by CRISPR is designed to last a lifetime, although confirmation will require years of follow-up.

          Get unlimited access to award-winning journalism and exclusive events.

          Subscribe Log In

          Wikipedia

          Jerome Adams on the need for new antivirals for Covid
          Jerome Adams on the need for new antivirals for Covid

          PaxlovidtabletsamplesbeinginspectedinFreiburg,Germany.PfizerviaAPTheU.S.Covid-19Public HealthEmergen

          read more
          Harvard scientists, with Google, unveil the most detailed brain map ever
          Harvard scientists, with Google, unveil the most detailed brain map ever

          AtHarvardUniversity,Dr.JeffreyLichtmanledanefforttoproducethemostdetailedmapofapieceofhumanbrainever

          read more
          Heart attack and stroke risk calculators need revising
          Heart attack and stroke risk calculators need revising

          AdobeForbusyprimarycarephysicianslikeme,anannualphysicalwitha27-year-oldmaleisablessing.Sincewe’real

          read more

          Harvard scientists, with Google, unveil the most detailed brain map ever

          AtHarvardUniversity,Dr.JeffreyLichtmanledanefforttoproducethemostdetailedmapofapieceofhumanbrainever