<code id='07946F8570'></code><style id='07946F8570'></style>

<acronym id='07946F8570'></acronym>

<center id='07946F8570'><center id='07946F8570'><tfoot id='07946F8570'></tfoot></center><abbr id='07946F8570'><dir id='07946F8570'><tfoot id='07946F8570'></tfoot><noframes id='07946F8570'>

<optgroup id='07946F8570'><strike id='07946F8570'><sup id='07946F8570'></sup></strike><code id='07946F8570'></code></optgroup>

<b id='07946F8570'><label id='07946F8570'><select id='07946F8570'><dt id='07946F8570'><span id='07946F8570'></span></dt></select></label></b><u id='07946F8570'></u>

~~<i id='07946F8570'><strike id='07946F8570'><tt id='07946F8570'><pre id='07946F8570'></pre></tt></strike></i>~~

Home» knowledge» knowledge

knowledge

knowledge

author：leisure time 2025-09-28 05:20:39 Page View：2

Hiram Secrist (left), who has Duchenne muscular dystrophy, with his mother, Kristen Secrist (center), and his grandmother, Terrie Jordan. Courtesy Secrist family

In mid-July, Kristen Secrist hopped on a call with her 5-year-old son’s doctor, who had urgent news: The first gene therapy had been approved for Duchenne muscular dystrophy. Her son, Hiram, would be a perfect candidate — if, she added, they could get him dosed in time.

The treatment was approved only for 4- and 5-year-olds. Hiram turned 6 in three weeks.

advertisement

“Oh, crap,” Secrist said to herself.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： Giraffe named Twiga, who was among the oldest cared for by humans, died at age 31 at East Texas zoo
Next article： State Dept. review finds Biden bears some blame for Afghanistan failures

knowledge

Food as medicine: CMS rules hamper 'prescribing' of fruits, veggies

Food as medicine: CMS rules hamper 'prescribing' of fruits, veggies

AdobeSometimes,anappleadayreallyisjustwhatthedoctorordered.Andforthepastseveralyears,organizationsli

Readout LOUD podcast: mifepristone case, GLP

WhogetstosuetheFDA?Ispharmacaughtinatradewar?Andwhatdoes“AF”standfor?Wecoverallthatandmorethisweekon

Biden outlines 'new path' to provide student loan relief after Supreme Court rejection

Biden outlines 'new path' to provide student loan relief after Supreme Court rejection

6:16PresidentJoeBidenspeaksintheRooseveltRoomoftheWhiteHouse,June30,2023.EvanVucci/APPresidentJoeBid

Readout Newsletter: Merck, Vertex, and Viking updates

MelEvans/APNewbiotechnewsletterlaunchingthisThursday. Don’tmissout.Hello,everyone.Damianherewithaloo

read more