<code id='730E239D9B'></code><style id='730E239D9B'></style>
    • <acronym id='730E239D9B'></acronym>
      <center id='730E239D9B'><center id='730E239D9B'><tfoot id='730E239D9B'></tfoot></center><abbr id='730E239D9B'><dir id='730E239D9B'><tfoot id='730E239D9B'></tfoot><noframes id='730E239D9B'>

    • <optgroup id='730E239D9B'><strike id='730E239D9B'><sup id='730E239D9B'></sup></strike><code id='730E239D9B'></code></optgroup>
        1. <b id='730E239D9B'><label id='730E239D9B'><select id='730E239D9B'><dt id='730E239D9B'><span id='730E239D9B'></span></dt></select></label></b><u id='730E239D9B'></u>
          <i id='730E239D9B'><strike id='730E239D9B'><tt id='730E239D9B'><pre id='730E239D9B'></pre></tt></strike></i>

          leisure time

          leisure time

          author:entertainment    Page View:38
          Gene therapy helped Conner Curran, right, walk, but as the drug fades, his family is supporting scientific efforts to allow him and other boys get a second dose. -- Biotech coverage from STAT
          Gene therapy helped Conner Curran (at right) walk, but as the drug fades, his family is supporting scientific efforts to allow him and other boys get a second dose. Courtesy Jess & Chris Curran

          In the beginning, Conner Curran ran up the stairs.

          It was a miraculous moment for him and his parents, Jess and Chris Curran. Just months before, contractors were in their New York home to install a motorized lift, while Jess tearfully explained that it wasn’t for a grandparent but for their 7-year-old son, who suffered from Duchenne muscular dystrophy and could barely haul himself up the steps.

          advertisement

          Then Conner was accepted as the first patient in Pfizer’s Duchenne gene therapy trial. Three weeks later, he could bound to the second floor. Soon, he could walk the two-plus miles to Goldberg’s, a local bagel shop. “I couldn’t do that before,” he told NPR in 2020. 

          Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

          GET STARTED Log In

          focus

          Jerome Adams on the need for new antivirals for Covid
          Jerome Adams on the need for new antivirals for Covid

          PaxlovidtabletsamplesbeinginspectedinFreiburg,Germany.PfizerviaAPTheU.S.Covid-19Public HealthEmergen

          read more
          Prior authorization reform is both possible and imperative
          Prior authorization reform is both possible and imperative

          AdobeImaginethisscene:Youareacancerpatientalreadynavigatingfearanduncertaintyaroundyourtreatment,whe

          read more
          Medical records are filled with copy
          Medical records are filled with copy

          AdobeIrecentlytookcareofapatientwhosemedicalrecordsincludedmultiplenotesaboutherpastopen-heartsurger

          read more

          Fight over Supreme Court dialysis ruling puts kidney patients at risk

          AdobeAssoonassheheardtheSupremeCourtdecision,LaVarneBurtonbegantoworry.AsCEOofthenonprofitAmericanKi