~~<i id='C47AE7E2F9'><strike id='C47AE7E2F9'><tt id='C47AE7E2F9'><pre id='C47AE7E2F9'></pre></tt></strike></i>~~

Home» knowledge» knowledge

knowledge

author：leisure time 2025-09-30 03:07:06 Page View：1

Hiram Secrist (left), who has Duchenne muscular dystrophy, with his mother, Kristen Secrist (center), and his grandmother, Terrie Jordan. Courtesy Secrist family

In mid-July, Kristen Secrist hopped on a call with her 5-year-old son’s doctor, who had urgent news: The first gene therapy had been approved for Duchenne muscular dystrophy. Her son, Hiram, would be a perfect candidate — if, she added, they could get him dosed in time.

The treatment was approved only for 4- and 5-year-olds. Hiram turned 6 in three weeks.

“Oh, crap,” Secrist said to herself.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： Some medical students still think black patients feel less pain
Next article： United colonoscopy coverage change 'may cost lives,' doctors say

explore

Anesthesiologist group: stop taking Ozempic before surgery

EspeciallyinthefirstweeksoftakingdrugslikeOzempic,foodstayslongerinthestomach—aprobleminsurgeries.Ad

Meta looks to target Twitter with a rival app called Threads

Theannouncementofthesocialmediaapp'Threads'isdisplayedinApple'sUSAppStoreseenonthescreenofasmartphon

How one medical school became remarkably diverse

ThefirstclassattheUniversityofCalifornia,Davismedicalschool,in1972,waspredominantlywhiteandmale.Chri

U.S. death rates show how politics are affecting public health

DrewAngerer/GettyImagesInanidealworld,publichealthwouldbeindependentofpolitics.YetrecenteventsintheU