~~<i id='3803BB6EED'><strike id='3803BB6EED'><tt id='3803BB6EED'><pre id='3803BB6EED'></pre></tt></strike></i>~~

Home» comprehensive» knowledge

knowledge

author：Wikipedia 2025-09-28 15:07:18 Page View：22

Hiram Secrist (left), who has Duchenne muscular dystrophy, with his mother, Kristen Secrist (center), and his grandmother, Terrie Jordan. Courtesy Secrist family

In mid-July, Kristen Secrist hopped on a call with her 5-year-old son’s doctor, who had urgent news: The first gene therapy had been approved for Duchenne muscular dystrophy. Her son, Hiram, would be a perfect candidate — if, she added, they could get him dosed in time.

The treatment was approved only for 4- and 5-year-olds. Hiram turned 6 in three weeks.

“Oh, crap,” Secrist said to herself.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED Log In

Previous article： David Liu startup to focus on CRISPR delivery
Next article： Virginia high school admissions case could be legal follow

leisure time

Food as medicine: CMS rules hamper 'prescribing' of fruits, veggies

AdobeSometimes,anappleadayreallyisjustwhatthedoctorordered.Andforthepastseveralyears,organizationsli

Change Healthcare cyberattack affects 25% of CVS/Aetna insurance claims

AdobeSomeofthecountry’sbiggesthealthinsurerssaidTuesdaythatuptoone-quarteroftheirclaimsarerunthrough

Dobbs anniversary: the lost opportunity of abortion as health care

NathanHoward/GettyImagesReflectingonthisfirstanniversaryoftheSupremeCourt’sdecisioninDobbstooverturn

Eli Lilly CEO gives to Mike Pence presidential super PAC

EliLillyDavidRicksisabigearlydonortoasuperPACsupportingMikePence.CarolynKaster/APWASHINGTON—DavidRic